RARECast

512 Folgen

1. Finding Answers for Undiagnosed Patients with Rare Genetic Diseases

   Vom: 16.9.2021
2. How a Familiar Face Can Lead to a Rare Disease Diagnosis

   Vom: 10.9.2021
3. Bringing the Trial to the Patient

   Vom: 2.9.2021
4. Targeting Rare and Chronic Kidney Diseases

   Vom: 26.8.2021
5. Addressing the Delivery Challenges of Genetic Medicines

   Vom: 19.8.2021
6. Targeting Tissues Throughout the Body with RNA Therapies

   Vom: 12.8.2021
7. Delivering Rare Disease Therapies to Patients in Need

   Vom: 5.8.2021
8. An Advocate's Journey through Diagnosis, Loss, and Hope

   Vom: 29.7.2021
9. Using Model Systems to Find Drugs to Repurpose for Rare Diseases

   Vom: 22.7.2021
10. How a Small and Young Foundation Catalyzed Research into a Rare Disease

    Vom: 16.7.2021
11. Overcoming the Limitations of Conventional Cell Engineering

    Vom: 8.7.2021
12. Experimental Therapy for Rare Endocrine Disorder Offers Hope of Improved Care

    Vom: 2.7.2021
13. Forging Gene Therapy Capacity and a Pipeline at the Same Time

    Vom: 24.6.2021
14. Using A Natural DNA Repair Process to Improve Genetic Medicines

    Vom: 18.6.2021
15. Empowering Rare Disease Patients with their Own Health Records

    Vom: 10.6.2021
16. Targeting CNS Disease with Gene Therapies

    Vom: 3.6.2021
17. A New Therapy Offers A Different Approach to Inhibiting the Complement System

    Vom: 28.5.2021
18. Bringing Aberrant Proteins Back into the Fold

    Vom: 20.5.2021
19. A Cat who Curates Rare Mice

    Vom: 13.5.2021
20. Putting the Patient at the Center of Rare Disease Clinical Trials

    Vom: 6.5.2021