RARECast

548 Folgen

1. Bridging the Gap Between Basic and Commercial Research for Rare Disease

   Vom: 26.5.2022
2. Stoking Functional Copies of Genes to Compensate for Mutated Ones

   Vom: 19.5.2022
3. Targeting ALS with Synergistic Combinations of Therapies

   Vom: 13.5.2022
4. How a Polish Rare Disease Organizations Is Helping Its Ukrainian Neighbors

   Vom: 5.5.2022
5. Powering a New Era of Genetic Medicine

   Vom: 28.4.2022
6. Searching for a Diagnosis

   Vom: 21.4.2022
7. A Novel Way to Deliver Rare Disease Therapies

   Vom: 14.4.2022
8. Bringing Diversity, Equity, and Inclusion to the Books We Read

   Vom: 7.4.2022
9. From Mila to Millions: Scaling N of 1 Therapies

   Vom: 31.3.2022
10. Genetically Modifying Patients’ Skin Cells to Treat Rare Diseases

    Vom: 24.3.2022
11. Targeting Rare, Immunologic Disorders

    Vom: 18.3.2022
12. Harnessing a Natural Mechanism to Silence Disease

    Vom: 10.3.2022
13. Advancing Precision Medicine with Patient Data

    Vom: 3.3.2022
14. Pregnancy and Motherhood for a Woman with SMA

    Vom: 24.2.2022
15. Steps to Improve Data Gathering of Rare Diseases

    Vom: 17.2.2022
16. Rare Patients Learn to Make Their Voices Heard

    Vom: 10.2.2022
17. Empowering Patient Organizations with Real-World Data

    Vom: 4.2.2022
18. A Healthcare Communications Student Gets an Education as a Patient

    Vom: 27.1.2022
19. Expanding the CRISPR Toolkit

    Vom: 21.1.2022
20. Marrying Antibodies to RNA Therapies to Target Previously Inaccessible Tissues and Cells

    Vom: 13.1.2022