RARECast

512 Folgen

1. Creating a Toolkit to Accelerate the Development of Gene Editing Therapies

   Vom: 29.4.2021
2. PTC Looks to Advanced Therapies

   Vom: 22.4.2021
3. Going to Extreme Lengths

   Vom: 15.4.2021
4. Everything’s up to Date in Kansas City, at Least When It Comes to Genomics

   Vom: 8.4.2021
5. Choosing the Right Viral Vector for a Gene Therapy

   Vom: 1.4.2021
6. A Software Platform to Give Patients the Tools to Build Treatments for Rare Genetic Diseases

   Vom: 25.3.2021
7. Side Effects: The Toll a Rare Disease Can Take on a Family in Pursuit of a Cure

   Vom: 19.3.2021
8. Realizing the Potential of CRISPR Gene Editing

   Vom: 12.3.2021
9. Understanding the Economic Toll of Rare Disease in the United States

   Vom: 4.3.2021
10. The Promise of Gene-Based Therapies for Neurodegenerative Conditions

    Vom: 25.2.2021
11. Moving Beyond Viral Vectors for Gene Therapies

    Vom: 19.2.2021
12. Acquisitions Help Jazz Build Toward Commercial Crescendo

    Vom: 12.2.2021
13. Powerful Gene Editing Approach Offers the Promise of Correcting a Range of Rare Diseases

    Vom: 5.2.2021
14. A Child's-Eye-View of Clinical Trials

    Vom: 29.1.2021
15. Using Nanoliposomes to Make Cancer Therapies Safer and More Effective

    Vom: 21.1.2021
16. Accelerating Treatments for Rare Disease through Data Sharing

    Vom: 14.1.2021
17. Treating the Root Cause of Sickle Cell Disease

    Vom: 8.1.2021
18. Targeting a Common Pathway in Genetic Forms of Obesity

    Vom: 30.12.2020
19. After Pruning Orchard, Gaspar Focuses on High Value Opportunities

    Vom: 23.12.2020
20. Writing a New Chapter of Genetic Medicine

    Vom: 17.12.2020