RARECast
Ein Podcast von RARECast - Donnerstags
Kategorien:
512 Folgen
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Advancing a Gene Therapy for a Rare and Fatal CNS Disorder
Vom: 30.3.2023 -
Addressing the Barriers to Patient Participation in Clinical Trials
Vom: 23.3.2023 -
A Venture Philanthropist Makes the Case for Advocates Taking Equity
Vom: 16.3.2023 -
Seeking a Sustainable Business Developing on N-of-1 Therapies
Vom: 9.3.2023 -
How One Drugmaker Reaches out to Communities at Greater Risk for Rare Heart Condition
Vom: 3.3.2023 -
A Next-Generation RNA Therapy Targets Telomere Disorders
Vom: 3.3.2023 -
BridgeBio Advances Therapy for Limb-Girdle Muscular Dystrophy that Started with Two Patient Families
Vom: 24.2.2023 -
Translating Urgency into Science
Vom: 16.2.2023 -
Empowering Ultra-Rare Disease Patients to Pursue the Discovery of Treatments
Vom: 10.2.2023 -
Why a Topical Cannabidiol Gel May Help Treat the Behavioral Symptoms of Fragile X
Vom: 2.2.2023 -
An Ultra-Rare Disease Drug Developer Tries to Navigate Regulatory Uncertainty
Vom: 26.1.2023 -
Powering Cells in People with Rare Mitochondrial Diseases
Vom: 19.1.2023 -
Powering Weakened and Stressed Cells in ALS to Function Better with Nanocrystal Therapy
Vom: 12.1.2023 -
Developing a New Class of Therapies Based on a Natural Cargo Carrier
Vom: 5.1.2023 -
Reaching Beyond the Limits of Enzyme Replacement Therapies with Gene Therapies
Vom: 29.12.2022 -
One Woman’s Journey as a Caregiver to a Husband with Frontotemporal Dementia
Vom: 22.12.2022 -
Treating Rare Endocrine Disorders with Therapeutic Peptides
Vom: 15.12.2022 -
Tackling the Pricing Challenges for Advanced Therapies for Rare Diseases
Vom: 8.12.2022 -
Addressing the Current Limitations of AAV Gene Therapies
Vom: 1.12.2022 -
Examining the Legislative Landscape for Rare Disease Drug Development
Vom: 24.11.2022
RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.