RARECast

548 Folgen

1. Improving the Function and Usability of Clothing for People with Disabilities

   Vom: 20.7.2023
2. Treating Cardiopulmonary Disease with Inhaled Targeted Therapies

   Vom: 13.7.2023
3. An Ally for the Undiagnosed Emerges

   Vom: 29.6.2023
4. A Patient-Driven Registry Focused on Health-Related Quality of Life Data

   Vom: 29.6.2023
5. Help for Rare Disease Patients That’s Just a Click Away

   Vom: 22.6.2023
6. Diagnosing Autism with a Single Strand of Hair

   Vom: 15.6.2023
7. Bringing Regenerative Medicine to a Rare Bone Condition in Children

   Vom: 8.6.2023
8. Bringing Precision to CRISPR-Based Genome Editing

   Vom: 1.6.2023
9. Capturing Patients’ Experience in Their Daily Lives

   Vom: 25.5.2023
10. From One to Many

    Vom: 18.5.2023
11. A Nasal Spray to Curb Excessive Eating in Prader-Willi

    Vom: 11.5.2023
12. How One Foundation Is Laying the Groundwork to Advance Treatments for an Ultra-Rare Disease

    Vom: 4.5.2023
13. Forging a New Path for Medicine

    Vom: 27.4.2023
14. Restoring Hearing through Gene Therapies

    Vom: 20.4.2023
15. Creating a Sustainable Reimbursement Model for Ultra-Rare Therapies

    Vom: 13.4.2023
16. Lumos Hopes Its Oral Alternative to HGH Will Fuel Its Growth

    Vom: 5.4.2023
17. Advancing a Gene Therapy for a Rare and Fatal CNS Disorder

    Vom: 30.3.2023
18. Addressing the Barriers to Patient Participation in Clinical Trials

    Vom: 23.3.2023
19. A Venture Philanthropist Makes the Case for Advocates Taking Equity

    Vom: 16.3.2023
20. Seeking a Sustainable Business Developing on N-of-1 Therapies

    Vom: 9.3.2023