RARECast

548 Folgen

1. Navigating the Challenges of Rare Disease Drug Development

   Vom: 31.5.2017
2. Accelerating Rare Disease Drug Discovery

   Vom: 24.5.2017
3. Experimental Rare Disease Therapy Wins New FDA Reg Med Designation

   Vom: 17.5.2017
4. How Rare Disease Patients Can Get their Voices Heard in Drug Discovery and Development

   Vom: 10.5.2017
5. One Patient's Difficult Road to a Rare Diagnosis

   Vom: 3.5.2017
6. How Researchers Diagnosed Four Patients with a Never-Before-Identified Rare Disease in a Day

   Vom: 26.4.2017
7. Stem Cell Gene Therapy Restores Immune System in Kids with SCID

   Vom: 19.4.2017
8. Rare Disease Advocates Push for Incentives to Drugmakers Pulled from Cures Act

   Vom: 12.4.2017
9. Non-Profit Drug Company Seeks to Advance Rare Disease Therapies

   Vom: 5.4.2017
10. Innovative Collaboration Model Drives Treatment for Rare Disease

    Vom: 29.3.2017
11. Girl with Rare Disease Inspires Search for Bone Marrow Donors

    Vom: 22.3.2017
12. A Quest for Tribe: Searching for Others with the Same Ultra-Rare Mutation

    Vom: 15.3.2017
13. Raising Awareness in a Town with a History of a Rare Disease

    Vom: 8.3.2017
14. Helping Rare Disease Patients Navigate the World of Information

    Vom: 1.3.2017
15. Overcoming the Challenges of Rare Disease Drug Development

    Vom: 22.2.2017
16. Moving Rare Disease Therapies from Hope to Reality

    Vom: 15.2.2017
17. Children’s National Launches First-of-its-Kind Rare Disease Center

    Vom: 8.2.2017
18. A Common Link in a Group of Rare Diseases Creates an Opportunity for Repurposing

    Vom: 1.2.2017
19. Sobi Works to Expand Rare Disease Indications for Its Drugs

    Vom: 25.1.2017
20. Why Rare Disease Patients Should Work Together to Address Common Concerns

    Vom: 18.1.2017