RARECast

548 Folgen

1. Deriving Rare Disease Therapies from Human Plasma

   Vom: 18.10.2017
2. Learning to Live with Purpose

   Vom: 11.10.2017
3. A Mother's Race to Find a Treatment for Her Daughter's Ultra-Rare Condition

   Vom: 4.10.2017
4. Screening for Rare Diseases

   Vom: 27.9.2017
5. A Look at the Changing World of Work for People with a Chronic Illness

   Vom: 20.9.2017
6. Aligning Interests in Rare Disease Partnerships

   Vom: 13.9.2017
7. A Veteran Venture Capitalist Discusses Investing in Rare Disease Drug Development

   Vom: 6.9.2017
8. A Patient Group Crafts Guidelines for Working with Pharma

   Vom: 30.8.2017
9. Bringing Innovation to Business Models for Rare Disease Drug Development

   Vom: 23.8.2017
10. Rethinking Accessibility and Dependency

    Vom: 16.8.2017
11. How Simon Wheatcroft, Blinded by a Rare Disease, Became an Ultramarathoner

    Vom: 9.8.2017
12. Spark Hoping Its Luxturna Will Become First FDA-Approved Gene Therapy

    Vom: 2.8.2017
13. What Rare Patient-Investors Can Learn From Venture Capitalists

    Vom: 26.7.2017
14. Novel Effort Delivers Failed DMD Drug to Former Clinical Trial Participants

    Vom: 19.7.2017
15. Centogene Seeks to Deliver Diagnoses to Rare Disease Patients Early

    Vom: 12.7.2017
16. Albireo Advances Pipeline for Rare Liver and Gastrointestinal Diseases

    Vom: 5.7.2017
17. aTyr Pharma Seeks to Modulate Activity in FSHD and Other Rare Disease

    Vom: 28.6.2017
18. Summit Pursues A Different Approach to Treating Duchenne

    Vom: 21.6.2017
19. Delivering Enzyme Replacement Therapies Across the Blood-Brain Barrier

    Vom: 14.6.2017
20. Sangamo Advances Gene Editing Therapies for Multiple Rare Diseases into the Clinic

    Vom: 7.6.2017