RARECast

548 Folgen

1. Addressing the Delivery Challenges of Genetic Medicines

   Vom: 19.8.2021
2. Targeting Tissues Throughout the Body with RNA Therapies

   Vom: 12.8.2021
3. Delivering Rare Disease Therapies to Patients in Need

   Vom: 5.8.2021
4. An Advocate's Journey through Diagnosis, Loss, and Hope

   Vom: 29.7.2021
5. Using Model Systems to Find Drugs to Repurpose for Rare Diseases

   Vom: 22.7.2021
6. How a Small and Young Foundation Catalyzed Research into a Rare Disease

   Vom: 16.7.2021
7. Overcoming the Limitations of Conventional Cell Engineering

   Vom: 8.7.2021
8. Experimental Therapy for Rare Endocrine Disorder Offers Hope of Improved Care

   Vom: 2.7.2021
9. Forging Gene Therapy Capacity and a Pipeline at the Same Time

   Vom: 24.6.2021
10. Using A Natural DNA Repair Process to Improve Genetic Medicines

    Vom: 18.6.2021
11. Empowering Rare Disease Patients with their Own Health Records

    Vom: 10.6.2021
12. Targeting CNS Disease with Gene Therapies

    Vom: 3.6.2021
13. A New Therapy Offers A Different Approach to Inhibiting the Complement System

    Vom: 28.5.2021
14. Bringing Aberrant Proteins Back into the Fold

    Vom: 20.5.2021
15. A Cat who Curates Rare Mice

    Vom: 13.5.2021
16. Putting the Patient at the Center of Rare Disease Clinical Trials

    Vom: 6.5.2021
17. Creating a Toolkit to Accelerate the Development of Gene Editing Therapies

    Vom: 29.4.2021
18. PTC Looks to Advanced Therapies

    Vom: 22.4.2021
19. Going to Extreme Lengths

    Vom: 15.4.2021
20. Everything’s up to Date in Kansas City, at Least When It Comes to Genomics

    Vom: 8.4.2021