RARECast

548 Folgen

1. Forging a Research Agenda for a Rare Disease

   Vom: 25.7.2018
2. Making the Journey from All-American Athlete to Rare Disease Advocate

   Vom: 18.7.2018
3. How Destiny Lamonte Learned to Advocate for Herself and Others

   Vom: 11.7.2018
4. Where the NIH Does Its Banking

   Vom: 5.7.2018
5. Making Sense of Nonsense Mutations

   Vom: 27.6.2018
6. Rewriting Faulty RNA

   Vom: 20.6.2018
7. Experimental Drug for "Elephant Man" Disease May Benefit Certain Cancers Too

   Vom: 13.6.2018
8. Programming Stem Cells to Protect Neurons in ALS and other Neurodegenerative Conditions

   Vom: 6.6.2018
9. Why a Topical, Off-the-Shelf, Gene Therapy May Hold Promise for a Rare Skin Condition

   Vom: 30.5.2018
10. An Ironman Champion with Cystic Fibrosis Discusses her Changing Relationship with Her Disease

    Vom: 23.5.2018
11. Why an Experimental Fragile X Drug May Treat a Range of Neurodegenerative Diseases

    Vom: 16.5.2018
12. The Case for a Daily Self-Injection to Treat Hemophilia

    Vom: 9.5.2018
13. Addressing the Challenges of R&D for Rare Cancer Therapies

    Vom: 2.5.2018
14. Learning to Communicate and Collaborate as a Patient Advocate

    Vom: 25.4.2018
15. Seeking Answers for Undiagnosed Patients

    Vom: 18.4.2018
16. When "Undiagnosed" Is Your Diagnosis

    Vom: 11.4.2018
17. The Decision to Get Tested for Huntington's Disease and How It Changed Seth Rotberg's Life

    Vom: 4.4.2018
18. Nonprofit Sees Need in Developing Gene Therapies for Inherited Eye Disesases

    Vom: 29.3.2018
19. Casting a Wider Net for Genetic Diseases

    Vom: 21.3.2018
20. Corbus Seeks to Quiet the Immune System in Chronic Conditions

    Vom: 14.3.2018