RARECast

512 Folgen

1. The Decision to Get Tested for Huntington's Disease and How It Changed Seth Rotberg's Life

   Vom: 4.4.2018
2. Nonprofit Sees Need in Developing Gene Therapies for Inherited Eye Disesases

   Vom: 29.3.2018
3. Casting a Wider Net for Genetic Diseases

   Vom: 21.3.2018
4. Corbus Seeks to Quiet the Immune System in Chronic Conditions

   Vom: 14.3.2018
5. Addressing the Challenges of Rare Disease Drug Development

   Vom: 7.3.2018
6. Giving Voice to Patients at the FDA

   Vom: 28.2.2018
7. Finding a Rare Friend

   Vom: 21.2.2018
8. Why a Sports Physical May Trigger a Doctor to Think About a Rare Diagnosis

   Vom: 14.2.2018
9. UPenn's Orphan Disease Center Takes a Rare Approach

   Vom: 7.2.2018
10. How Patients Can Accelerate Translational Research in Rare Disease

    Vom: 31.1.2018
11. Notre Dame Center Leverages Commonalities of Rare and Neglected Diseases

    Vom: 24.1.2018
12. GalXC Quest: Dicerna Bets on Its Unqiue Approach to RNAi

    Vom: 17.1.2018
13. Pharnext Takes a Unique Twist on Repurposing Drugs for Rare Diseases

    Vom: 10.1.2018
14. uniQure Seeks to Find Elusive Market Success with Hemophilia B Gene Therapy

    Vom: 3.1.2018
15. Savara Advances Pipeline of Inhaled Therapeutics for Rare Lung Diseases

    Vom: 27.12.2017
16. Why the Microbiome May Provide a Novel Approach to Treating Certain Rare Diseases

    Vom: 20.12.2017
17. FDA Outlines a Collaborative Approach for Pediatric Rare Disease Trials

    Vom: 13.12.2017
18. Why Patient-Centred Outcomes Are Critical to Rare Disease Drug Trials

    Vom: 6.12.2017
19. What the FDA's New Framework Means for Regenerative Therapies

    Vom: 29.11.2017
20. Measuring the Value of Therapies for Ultra-Rare Diseases

    Vom: 22.11.2017