RARECast
Ein Podcast von RARECast - Donnerstags
548 Folgen
-
A Heart Attack that Led to a Rare Disease Diagnosis
Vom: 30.1.2025 -
Targeting Rare Liver Diseases with Gene Editing Therapies
Vom: 23.1.2025 -
Using AI to De-Risk Rare Disease Drug Development
Vom: 16.1.2025 -
Addressing a Growing Demand for Plasma-Derived Therapies
Vom: 9.1.2025 -
Empowering Patients with Data to Drive Drug Development
Vom: 2.1.2025 -
How Advocates Are Advancing a Treatment for an Ultra-Rare Disease
Vom: 26.12.2024 -
Engineering B Cells to Produce Therapeutic Proteins
Vom: 19.12.2024 -
A Pipeline Win as BridgeBio Learns to Balance Theory with Practice
Vom: 12.12.2024 -
Considering What It Will Take for Payers to Embrace Advances in Sequencing
Vom: 5.12.2024 -
Finding Strength
Vom: 27.11.2024 -
A Non-Profit Works to Advance a DMD Gene Therapy
Vom: 21.11.2024 -
Accepting What We Can’t Understand
Vom: 14.11.2024 -
A Gene Therapy Company Born from a Father’s Efforts to Save his Daughter
Vom: 7.11.2024 -
Lowering Barriers to Clinical Trial Participation with Do-It-Yourself Blood Sample Collection
Vom: 31.10.2024 -
Scaling N-of-1 Therapies to Viability
Vom: 24.10.2024 -
Building Gene Therapies that Address Gain and Loss of Function Simultaneously
Vom: 17.10.2024 -
How One Woman Climbed from Patient to Advocate
Vom: 10.10.2024 -
Shortening the Diagnostic Odyssey
Vom: 3.10.2024 -
Making Exomes More Revealing
Vom: 26.9.2024 -
How One Patient Organization Catalyzed Drug Development
Vom: 19.9.2024
RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.
