RARECast

512 Folgen

1. Aspa Therapeutics Forges Gene Therapy for Rare Neurological Condition

   Vom: 9.1.2019
2. How Patient-Led Collaborations Are Transforming Rare Disease Drug Discovery and Development

   Vom: 2.1.2019
3. Sobi Expands Its Immunology Franchise with HLH Drug Approval

   Vom: 27.12.2018
4. Learning to Thrive

   Vom: 19.12.2018
5. Late-Stage Trial Underway for Treatment of Rare Obesity Disorder

   Vom: 12.12.2018
6. RegenxBio Bets Its Gene Therapy Technology Provides Competitive Edge

   Vom: 5.12.2018
7. The Potential for Digital Health Technologies to Transform Clinical Trials

   Vom: 28.11.2018
8. Matching Volunteers to Rare Disease Organizations in Need

   Vom: 21.11.2018
9. How One Rare Disease Organization Used Technology to Provide Greater Patient Insight to FDA

   Vom: 14.11.2018
10. The Potentially Deadly Consequences of an Oversight in Newborn Screening Tests

    Vom: 7.11.2018
11. Advancing a New Approach to Sickle Cell Disease

    Vom: 31.10.2018
12. Conquering Life with a Rare Disease

    Vom: 24.10.2018
13. Why Rare Disease Drug Developers Need Regular Interaction with the FDA

    Vom: 17.10.2018
14. Making the Case for an FDA Rare Disease Center of Excellence

    Vom: 10.10.2018
15. An Elite Runner Makes a Cross-Canada Trek for His Son and Rare Disease

    Vom: 3.10.2018
16. How Rare Disease Advocates Can Get The Most out of Collaborations

    Vom: 26.9.2018
17. Establishing Clinical Standards for a Rare Disease

    Vom: 19.9.2018
18. Teen Rare Disease Advocate Fights the Condition That Took His Brother's Life

    Vom: 12.9.2018
19. Addressing the Emotional Toll of Rare Diseases

    Vom: 5.9.2018
20. Forging a Research Agenda for a Rare Disease

    Vom: 29.8.2018