RARECast

548 Folgen

1. Fighting for Other People's Children

   Vom: 18.9.2019
2. A Doctor's Quest to Cure His Own Rare Disease

   Vom: 11.9.2019
3. Susannah Cahalan and her Month of Madness

   Vom: 4.9.2019
4. The Benefits Support Groups Offer Rare Disease Patients

   Vom: 29.8.2019
5. Targeting the Epigenetic Drivers of Cancer

   Vom: 21.8.2019
6. Tackling Kidney Diseases with Orally-Delivered Enzymes

   Vom: 14.8.2019
7. Giving Voice to Patients through Data

   Vom: 8.8.2019
8. Seeking to Halt and Reverse Fibrotic Diseases

   Vom: 31.7.2019
9. Addressing the Complexities of Rare Disease with Centers of Excellence

   Vom: 24.7.2019
10. Using Cell Therapies to Restore Power in Mitochondrial Diseases

    Vom: 17.7.2019
11. Passage Bio Betting on Penn Connection to Give It an Edge in Developing Gene Therapies

    Vom: 10.7.2019
12. Finding Appropriate Endpoints and Measures for Rare Eye Diseases

    Vom: 3.7.2019
13. Marrying Antibodies and Oligonucleotides to Target Genetic Medicine

    Vom: 26.6.2019
14. What Rare Disease Patients Should Understand about Genetics

    Vom: 19.6.2019
15. Program Seeks to Drive Collaborative Research Model Among Rare Disease Groups

    Vom: 12.6.2019
16. A Gene Hunter Becomes a Drug Hunter Too

    Vom: 5.6.2019
17. The Psychological Toll Rare Diseases Can Have on Healthy Siblings

    Vom: 29.5.2019
18. Blood Test Can Provide Earlier Diagnosis of Autism Spectrum Disorder

    Vom: 22.5.2019
19. Understanding the Role of Natural History Studies in Clinical Trials

    Vom: 15.5.2019
20. How Two Mothers Discovered That a Drug for One Rare Disorder Might Benefit Another

    Vom: 8.5.2019