RARECast

512 Folgen

1. Targeting Hormone Dysregulation in Prader-Willi Syndrome

   Vom: 4.3.2020
2. Rare Disease Advocates Take to the Hill

   Vom: 25.2.2020
3. Targeting a Common Link in Otherwise Different Rare Diseases

   Vom: 19.2.2020
4. Bringing Clinical Trials to Patients

   Vom: 12.2.2020
5. Crowdsourcing Therapeutic Approaches for an Ultra-Rare Disease

   Vom: 5.2.2020
6. Delivering Oligonucleotide Therapies to Any Cell Type

   Vom: 29.1.2020
7. Protalix Looks Beyond Biobetters

   Vom: 22.1.2020
8. Driving N-of-1 Therapies for Ultra-Rare Disease Patients

   Vom: 15.1.2020
9. Cutting the Time and Cost of Drug Discovery with MicroOrgans

   Vom: 8.1.2020
10. Acquisition Combines Two Pipelines for Rare Skin Diseases

    Vom: 2.1.2020
11. Programming Cells to Produce Neuroprotective Factors to Treat ALS

    Vom: 26.12.2019
12. Origin's Rapid Path to Seek Approval for Treatment of Ultra-Rare Metabolic Condition

    Vom: 18.12.2019
13. Developing a Common Language for Rare Diseases

    Vom: 11.12.2019
14. Why Payers Lag Drug Developers and Regulators in Embracing Real-World Evidence

    Vom: 4.12.2019
15. How a Brother's Love Is Forging a Path for Customized Therapies for Rare Disease Patients

    Vom: 27.11.2019
16. Addressing the Barriers to Accessing Experimental Therapies

    Vom: 20.11.2019
17. A Journey to Advocacy

    Vom: 13.11.2019
18. Turning Chronic Illness into a Fashion Statement

    Vom: 6.11.2019
19. Connecting Young Adults with Rare and Chronic Conditions

    Vom: 30.10.2019
20. Helping Caregivers Care for Themselves

    Vom: 23.10.2019