After Driving an N-of-1 Therapy for Her Son, an Advocate Turns to Helping Others

Yiwei She, founder of the TNPO2 Foundation, discusses how her family was able to treat her son Leo with an experimental ASO with relative speed, the work the TNPO2 Foundation is doing to accelerate the diagnosis of other children with ultra-rare conditions, and its efforts to find accessible and affordable pathways to treatments for others.