Rare disease market access - strategic and tactical challenges facing orphan medicines entering Europe

We explore the challenges facing orphan medicines and other innovative rare disease treatments looking to achieve market access in Europe.Orphan medicines and rare disease treatments are faced with a complex, ever-changing market landscape. These treatments also face unique tactical challenges on the route to securing market access.Here we bring together specialists from our global market access (Rob Taaffe), systematic review (Regina Leadley), and health economic (Calum Jones) teams to explo...